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Trial details imported from ClinicalTrials.gov

For full trial details, please see the original record at https://clinicaltrials.gov/study/NCT07008118




Registration number
NCT07008118
Ethics application status
Date submitted
29/05/2025
Date registered
6/06/2025
Date last updated
10/07/2025

Titles & IDs
Public title
A Study to Evaluate INCA035784 in Participants With Myeloproliferative Neoplasms
Scientific title
A Phase 1, Open-Label, Multicenter Study of INCA035784 in Participants With Myeloproliferative Neoplasms
Secondary ID [1] 0 0
INCA035784-101
Universal Trial Number (UTN)
Trial acronym
Linked study record

Health condition
Health condition(s) or problem(s) studied:
Myeloproliferative Neoplasms 0 0
Condition category
Condition code
Cancer 0 0 0 0
Leukaemia - Acute leukaemia
Cancer 0 0 0 0
Leukaemia - Chronic leukaemia

Intervention/exposure
Study type
Interventional
Description of intervention(s) / exposure
Treatment: Drugs - INCA035784

Experimental: Part 1a: Dose escalation - INCA035784 will be administered at a protocol defined starting regimen in 28-day cycles as monotherapy to identify the maximum tolerated dose (MTD) and/or recommended dose for expansion (RDE\[s\]). Participants with myeloproliferative neoplasm (MPN) will enroll in this group.

Experimental: Part 1b: Dose expansion - INCA035784 will be administered as monotherapy at the RDE(s) identified during Part 1a. Participants with myeloproliferative neoplasm (MPN) will enroll in this group.


Treatment: Drugs: INCA035784
INCA035784 will be administered at protocol defined dose.

Intervention code [1] 0 0
Treatment: Drugs
Comparator / control treatment
Control group

Outcomes
Primary outcome [1] 0 0
Number of participants with Dose Limiting Toxicities (DLTs)
Timepoint [1] 0 0
Up to 28 days
Primary outcome [2] 0 0
Number of participants with Treatment-emergent Adverse Events (TEAEs)
Timepoint [2] 0 0
Up to approximately 2 years and 90 days
Primary outcome [3] 0 0
Number of participants with TEAEs leading to treatment interruption, discontinuation, or delay
Timepoint [3] 0 0
Up to approximately 2 years and 90 days
Secondary outcome [1] 0 0
Number of participants with TEAEs leading to dose modification or discontinuation
Timepoint [1] 0 0
Up to approximately 2 years and 90 days
Secondary outcome [2] 0 0
Participants with MF: Response using the revised International Working Group for Myelofibrosis Research and Treatment (IWG-MRT) and European LeukemiaNet (ELN) response criteria for myelofibrosis (MF)
Timepoint [2] 0 0
Up to approximately 2 years and 90 days
Secondary outcome [3] 0 0
Participants with essential thrombocythemia (ET): Response using the revised IWG-MRT and ELN response criteria for ET
Timepoint [3] 0 0
Up to approximately 2 years and 90 days
Secondary outcome [4] 0 0
Participants with myelodysplastic syndrome (MDS)/MPN: Response using the revised IWG-MRT response criteria for MDS/MPN
Timepoint [4] 0 0
Up to approximately 2 years and 90 days
Secondary outcome [5] 0 0
Participants with symptomatic anemia: Anemia response
Timepoint [5] 0 0
Up to approximately 2 years and 90 days
Secondary outcome [6] 0 0
Participants with spleen volume (SV) = 450 mL at baseline: Percentage of participants achieving spleen volume reduction of = 35% (SVR35)
Timepoint [6] 0 0
Week 12 and Week 24
Secondary outcome [7] 0 0
Participants with SV = 450 mL at baseline: Percentage of participants achieving spleen volume reduction of = 25% (SVR25)
Timepoint [7] 0 0
Week 12 and Week 24
Secondary outcome [8] 0 0
Percentage of participants achieving = 50% reduction from baseline of total symptom score (TSS)
Timepoint [8] 0 0
Week 12 and Week 24
Secondary outcome [9] 0 0
Mean change from baseline in TSS
Timepoint [9] 0 0
Week 12 and Week 24
Secondary outcome [10] 0 0
Pharmacokinetics Parameter (PK): Cmax of INCA035784
Timepoint [10] 0 0
Up to approximately 2 years and 90 days
Secondary outcome [11] 0 0
Pharmacokinetics Parameter: Tmax of INCA035784
Timepoint [11] 0 0
Up to approximately 2 years and 90 days
Secondary outcome [12] 0 0
Pharmacokinetics Parameter: Cmin of INCA035784
Timepoint [12] 0 0
Up to approximately 2 years and 90 days
Secondary outcome [13] 0 0
Pharmacokinetics Parameter: AUC(0-t) of INCA035784
Timepoint [13] 0 0
Up to approximately 2 years and 90 days
Secondary outcome [14] 0 0
Pharmacokinetics Parameter: AUC 0-8 of INCA035784
Timepoint [14] 0 0
Up to approximately 2 years and 90 days
Secondary outcome [15] 0 0
Pharmacokinetics Parameter: CL of INCA035784
Timepoint [15] 0 0
Up to approximately 2 years and 90 days
Secondary outcome [16] 0 0
Pharmacokinetics Parameter: Vz of INCA035784
Timepoint [16] 0 0
Up to approximately 2 years and 90 days
Secondary outcome [17] 0 0
Pharmacokinetics Parameter: t1/2 of INCA035784
Timepoint [17] 0 0
Up to approximately 2 years and 90 days

Eligibility
Key inclusion criteria
* Age 18 years or older at the time of signing the ICF
* ECOG performance status of 0 to 1 for the dose escalation (Part 1a) and 0 to 2 for the dose expansion (Part 1b)
* Documented CALR exon-9 mutation
* Confirmed diagnosis of MPN according to the 2022 ICC criteria:

* DIPSS+ intermediate-2/high-risk MF with prior JAKi, <20% blasts, and measurable spleen
* High-risk ET with platelets >450×10?/L
* Resistant, refractory, intolerant, or has lost response to =1 prior line of therapy for MF and =2 prior lines for ET
* No prior stem cell transplant and none planned within 6 months
* Minimum Laboratory Requirements:

* Platelet count =50 × 10?/L
* Absolute neutrophil count =1 × 10?/L
* International normalized ratio (INR) and activated partial thromboplastin time (aPTT) =1.5 × upper limit of normal (ULN), unless receiving vitamin K antagonists
* Alanine aminotransferase (ALT) and aspartate aminotransferase (AST) <2.5 × ULN
* Total bilirubin <2 × ULN
* Estimated creatinine clearance >45 or >30 mL/min (depending on study part)
Minimum age
18 Years
Maximum age
No limit
Sex
Both males and females
Can healthy volunteers participate?
No
Key exclusion criteria
* Major bleeding or thrombosis (e.g., stroke, DVT, PE) within the past 3 months
* Active or high-risk HBV, HCV, or HIV infection, or other chronic active infections requiring systemic treatment
* Active invasive cancer within the past 2 years, except certain early-stage or low-risk cancers (e.g., resected skin, cervical, thyroid, or prostate cancer)
* Pregnant or unwilling to avoid pregnancy or fathering a child during the study and for a defined period after the last dose.

Other protocol-defined Inclusion/Exclusion Criteria may apply.

Study design
Purpose of the study
Treatment
Allocation to intervention
Non-randomised trial
Procedure for enrolling a subject and allocating the treatment (allocation concealment procedures)
Methods used to generate the sequence in which subjects will be randomised (sequence generation)
Masking / blinding
Open (masking not used)
Who is / are masked / blinded?



Intervention assignment
Other
Other design features
Phase
Phase 1
Type of endpoint/s
Statistical methods / analysis

Recruitment
Recruitment status
Recruiting
Data analysis
Reason for early stopping/withdrawal
Other reasons
Date of first participant enrolment
Anticipated
Actual
Date of last participant enrolment
Anticipated
Actual
Date of last data collection
Anticipated
Actual
Sample size
Target
Accrual to date
Final
Recruitment in Australia
Recruitment state(s)
NSW,SA,VIC,WA
Recruitment hospital [1] 0 0
Macquarie University Hospital - Sydney
Recruitment hospital [2] 0 0
Royal Adelaide Hospital - Adelaide
Recruitment hospital [3] 0 0
The Alfred Hospital - Melbourne
Recruitment hospital [4] 0 0
Linear Clinical Research - Nedlands
Recruitment postcode(s) [1] 0 0
02109 - Sydney
Recruitment postcode(s) [2] 0 0
05000 - Adelaide
Recruitment postcode(s) [3] 0 0
03004 - Melbourne
Recruitment postcode(s) [4] 0 0
06009 - Nedlands
Recruitment outside Australia
Country [1] 0 0
United States of America
State/province [1] 0 0
California
Country [2] 0 0
United States of America
State/province [2] 0 0
Colorado
Country [3] 0 0
United States of America
State/province [3] 0 0
Illinois
Country [4] 0 0
United States of America
State/province [4] 0 0
Maryland
Country [5] 0 0
United States of America
State/province [5] 0 0
Massachusetts
Country [6] 0 0
United States of America
State/province [6] 0 0
New York
Country [7] 0 0
United States of America
State/province [7] 0 0
North Carolina
Country [8] 0 0
United States of America
State/province [8] 0 0
Utah
Country [9] 0 0
United States of America
State/province [9] 0 0
Wisconsin

Funding & Sponsors
Primary sponsor type
Commercial sector/industry
Name
Incyte Corporation
Address
Country

Ethics approval
Ethics application status

Summary
Brief summary
Trial website
Trial related presentations / publications
Public notes

Contacts
Principal investigator
Name 0 0
Incyte Medical Monitor
Address 0 0
Incyte Corporation
Country 0 0
Phone 0 0
Fax 0 0
Email 0 0
Contact person for public queries
Name 0 0
Incyte Corporation Call Center (US)
Address 0 0
Country 0 0
Phone 0 0
1.855.463.3463
Fax 0 0
Email 0 0
Contact person for scientific queries

Data sharing statement
Will individual participant data (IPD) for this trial be available (including data dictionaries)?
No
No/undecided IPD sharing reason/comment


What supporting documents are/will be available?

No Supporting Document Provided


Results publications and other study-related documents

No documents have been uploaded by study researchers.