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Trial details imported from ClinicalTrials.gov

For full trial details, please see the original record at https://clinicaltrials.gov/study/NCT06867094




Registration number
NCT06867094
Ethics application status
Date submitted
4/03/2025
Date registered
10/03/2025
Date last updated
3/07/2025

Titles & IDs
Public title
A Study to Investigate Efficacy and Safety of SAR441566 in Patients With Ulcerative Colitis
Scientific title
A Phase 2, Multinational, Multicenter, Randomized, Double-blind, Placebo-controlled, Dose-ranging Study to Evaluate the Efficacy and Safety of SAR441566 in Adults With Moderate-to-severe Ulcerative Colitis
Secondary ID [1] 0 0
U1111-1308-9729
Secondary ID [2] 0 0
DRI17822
Universal Trial Number (UTN)
Trial acronym
SPECIFI-UC
Linked study record

Health condition
Health condition(s) or problem(s) studied:
Colitis Ulcerative 0 0
Condition category
Condition code
Oral and Gastrointestinal 0 0 0 0
Other diseases of the mouth, teeth, oesophagus, digestive system including liver and colon
Inflammatory and Immune System 0 0 0 0
Other inflammatory or immune system disorders
Oral and Gastrointestinal 0 0 0 0
Inflammatory bowel disease

Intervention/exposure
Study type
Interventional
Description of intervention(s) / exposure
Treatment: Drugs - SAR441566
Treatment: Drugs - SAR441566 matching Placebo

Experimental: SAR441566 dose regimen 1 - Participants will receive SAR441566 dose regimen 1

Experimental: SAR441566 dose regimen 2 - Participants will receive SAR441566 dose regimen 2

Experimental: SAR441566 dose regimen 3 - Participants will receive SAR441566 dose regimen 3

Placebo comparator: Placebo - Participants will receive SAR441566-matching placebo


Treatment: Drugs: SAR441566
Pharmaceutical form: Tablet Route of administration: Oral

Treatment: Drugs: SAR441566 matching Placebo
Pharmaceutical form: Tablet Route of administration: Oral

Intervention code [1] 0 0
Treatment: Drugs
Comparator / control treatment
Control group

Outcomes
Primary outcome [1] 0 0
Proportion of participants achieving clinical remission at Week 12 by modified Mayo Score (mMS)
Timepoint [1] 0 0
Week 12
Secondary outcome [1] 0 0
Proportion of participants achieving clinical response at Week 12 by modified Mayo Score (mMS)
Timepoint [1] 0 0
Week 12
Secondary outcome [2] 0 0
Proportion of participants achieving clinical response at Week 12 by full Mayo score (MS)
Timepoint [2] 0 0
Week 12
Secondary outcome [3] 0 0
Proportion of participants achieving clinical remission at Week 12 by full Mayo score (MS)
Timepoint [3] 0 0
Week 12
Secondary outcome [4] 0 0
Proportion of participants achieving the combination of patient-reported outcome 2 (PRO2) remission and endoscopic remission at Week 12
Timepoint [4] 0 0
Week 12
Secondary outcome [5] 0 0
Proportion of participants achieving endoscopic remission at Week 12
Timepoint [5] 0 0
Week 12
Secondary outcome [6] 0 0
Change from baseline in PRO2 from randomization to Week 12
Timepoint [6] 0 0
From Baseline to Week 12
Secondary outcome [7] 0 0
Proportion of participants achieving endoscopic response at Week 12
Timepoint [7] 0 0
Week 12
Secondary outcome [8] 0 0
Proportion of participants achieving endoscopic improvement at Week 12
Timepoint [8] 0 0
Week 12
Secondary outcome [9] 0 0
Proportion of participants achieving HEMI at Week 12
Timepoint [9] 0 0
Week 12
Secondary outcome [10] 0 0
Plasma predose concentrations of SAR441566 at selected visits
Timepoint [10] 0 0
Up to Week 52
Secondary outcome [11] 0 0
Plasma postdose concentrations of SAR441566 at selected visits
Timepoint [11] 0 0
Up to Week 52
Secondary outcome [12] 0 0
Number of participants with any treatment-emergent adverse events (TEAEs) during induction and maintenance treatment period
Timepoint [12] 0 0
Up to Week 52
Secondary outcome [13] 0 0
Number of participants with any treatment-emergent adverse events (TEAEs) during open-label treatment period
Timepoint [13] 0 0
From Week 12 to Week 52
Secondary outcome [14] 0 0
Proportion achieving Inflammatory Bowel Disease Questionnaire (IBDQ) remission at Week 12
Timepoint [14] 0 0
Week 12
Secondary outcome [15] 0 0
Proportion of participants achieving Inflammatory Bowel Disease Questionnaire (IBDQ) response at Week 12
Timepoint [15] 0 0
Week 12
Secondary outcome [16] 0 0
Inflammatory Bowel Disease Questionnaire (IBDQ) response is defined as an increase from baseline in the total IBDQ score in the range of 16 to 32 points.
Timepoint [16] 0 0
Week 12

Eligibility
Key inclusion criteria
Participants are eligible to be included in the study only if all of the following criteria apply:

* Male or female participants aged 18 to 75 years inclusive, at the time of signing the informed consent
* Participants who have clinical evidence of active UC for =3 months before screening and confirmed by endoscopy during the screening period
* Active moderate-to-severe UC at screening as defined by a modified Mayo Score (mMS) of 5 to 9 (without the Physician global Assessment (PGA), with a minimum rectal bleeding (RB) subscore =1, a minimum stool frequency (SF) subscore =1, a mMES =2 confirmed by central reader, a minimum sum of all subscores of 5, and a disease extent >15 cm from the anal verge
* Must have received prior treatment for UC (either "a" or "b" below or combination of both):

1. No prior exposure to Advanced Therapy (AT), but having inadequate response to, loss of response to or intolerance to standard treatment with any of the following compounds: 5-ASA, 6-MP, AZA, MTX, oral or intravenous (IV) corticosteroids or history of corticosteroid dependence (defined an inability to successfully taper corticosteroids without recurrence of UC) OR
2. Inadequate response to, loss of response to or intolerance to treatment with =1 approved AT such as a biologic agent (such as TNF antagonists, anti-integrin other than natalizumab, anti-IL-12/23, anti-IL-23, or experimental biologic UC therapeutics), or a small molecule (such as a JAKi or S1PRm) for UC
* Contraceptive use by men and women should be consistent with local regulations regarding the methods of contraception for those participating in clinical studies.
Minimum age
18 Years
Maximum age
75 Years
Sex
Both males and females
Can healthy volunteers participate?
No
Key exclusion criteria
Participants are excluded from the study if any of the following criteria apply:

* Participants with active CD, indeterminate colitis, ischemic colitis, microscopic colitis
* Participants with the following ongoing known complications of UC: fulminant colitis, toxic megacolon, or any other manifestation that might require bowel surgery while enrolled in the study
* Participant with prior colectomy, ostomy or ileoanal pouch, or anticipated colectomy during their participation in the study
* Participants with fecal sample positive for ova or parasites, bacterial pathogens, or positive for Clostridium difficile B toxin in stools
* Participants with active tuberculosis (TB) or a history of incompletely treated active TB or latent TB infection per local guidelines
* Participants with Positive Hepatitis B surface antigen (HBsAg), or Hepatitis B core antibody (HBcAb) and/or Hepatitis C virus antibody (HCVAb) at the screening visit
* Participants with any other active, chronic or recurrent infection, including recurrent or disseminated herpes zoster or disseminated herpes simplex
* Participants with a known history of human immunodeficiency virus (HIV) infection or positive HIV-1 or HIV-2 serology at screening
* Participants presenting with active malignancies, lymphoproliferative disease, or recurrence of either, within the 5 years before screening
* If the participant has extensive colitis for =8 years or disease limited to left side of colon (ie, distal to splenic flexure) for >10 years, regardless of age, a colonoscopy within 1 year of the screening visit is required to survey for dysplasia. Participants with dysplasia or cancer identified on biopsies will be excluded.
* Female participants who is pregnant, breastfeeding, or is considering becoming pregnant during the study or within 3 months after the last dose of study drug
* Infection(s) requiring treatment with IV anti-infectives within 30 days prior to the screening visit or oral/intramuscular anti-infectives within 14 days prior to the screening visit
* Participants requiring or receiving any parental nutrition and/or exclusive enteral nutrition
* Participants who received cyclosporine, tacrolimus, mycophenolate mofetil, or thalidomide within 30 days prior to screening
* Participants who received fecal microbial transplantation within 30 days prior to screening
* Participants who have ever been exposed to natalizumab (Tysabri®) or oral carotegrast methyl (Carogra®)
* Participants who received IV corticosteroids within 14 days prior to screening or during screening period
* Screening laboratory and other analyses show abnormal results.

The above information is not intended to contain all considerations relevant to a participant's potential participation in a clinical trial.

Study design
Purpose of the study
Treatment
Allocation to intervention
Randomised controlled trial
Procedure for enrolling a subject and allocating the treatment (allocation concealment procedures)
Methods used to generate the sequence in which subjects will be randomised (sequence generation)
Masking / blinding
Blinded (masking used)
Who is / are masked / blinded?
The people receiving the treatment/s
The people administering the treatment/s
The people assessing the outcomes
The people analysing the results/data
Intervention assignment
Parallel
Other design features
Phase
Phase 2
Type of endpoint/s
Statistical methods / analysis

Recruitment
Recruitment status
Recruiting
Data analysis
Reason for early stopping/withdrawal
Other reasons
Date of first participant enrolment
Anticipated
Actual
Date of last participant enrolment
Anticipated
Actual
Date of last data collection
Anticipated
Actual
Sample size
Target
Accrual to date
Final
Recruitment in Australia
Recruitment state(s)
QLD
Recruitment hospital [1] 0 0
Investigational Site Number : 0360001 - Mackay
Recruitment postcode(s) [1] 0 0
4740 - Mackay
Recruitment outside Australia
Country [1] 0 0
United States of America
State/province [1] 0 0
Arizona
Country [2] 0 0
United States of America
State/province [2] 0 0
Connecticut
Country [3] 0 0
United States of America
State/province [3] 0 0
Florida
Country [4] 0 0
United States of America
State/province [4] 0 0
Illinois
Country [5] 0 0
United States of America
State/province [5] 0 0
Michigan
Country [6] 0 0
United States of America
State/province [6] 0 0
New York
Country [7] 0 0
United States of America
State/province [7] 0 0
Pennsylvania
Country [8] 0 0
United States of America
State/province [8] 0 0
Texas
Country [9] 0 0
United States of America
State/province [9] 0 0
Washington
Country [10] 0 0
Argentina
State/province [10] 0 0
Buenos Aires
Country [11] 0 0
Belgium
State/province [11] 0 0
Gent
Country [12] 0 0
Belgium
State/province [12] 0 0
Leuven
Country [13] 0 0
Canada
State/province [13] 0 0
Nova Scotia
Country [14] 0 0
Canada
State/province [14] 0 0
Québec City
Country [15] 0 0
Chile
State/province [15] 0 0
Reg Metropolitana De Santiago
Country [16] 0 0
Czechia
State/province [16] 0 0
Olomouc
Country [17] 0 0
Japan
State/province [17] 0 0
Chiba
Country [18] 0 0
Japan
State/province [18] 0 0
Niigata
Country [19] 0 0
Japan
State/province [19] 0 0
Hiroshima

Funding & Sponsors
Primary sponsor type
Commercial sector/industry
Name
Sanofi
Address
Country

Ethics approval
Ethics application status

Summary
Brief summary
Trial website
Trial related presentations / publications
Public notes

Contacts
Principal investigator
Name 0 0
Address 0 0
Country 0 0
Phone 0 0
Fax 0 0
Email 0 0
Contact person for public queries
Name 0 0
Trial Transparency email recommended (Toll free for US & Canada)
Address 0 0
Country 0 0
Phone 0 0
800-633-1610
Fax 0 0
Email 0 0
Contact person for scientific queries

Data sharing statement
Will individual participant data (IPD) for this trial be available (including data dictionaries)?
Yes
What data in particular will be shared?
Qualified researchers may request access to patient level data and related study documents including the clinical study report, study protocol with any amendments, blank case report form, statistical analysis plan, and dataset specifications. Patient level data will be anonymized and study documents will be redacted to protect the privacy of trial participants. Further details on Sanofi's data sharing criteria, eligible studies, and process for requesting access can be found at: https://vivli.org
When will data be available (start and end dates)?
Available to whom?
Available for what types of analyses?
How or where can data be obtained?


What supporting documents are/will be available?

No Supporting Document Provided


Results publications and other study-related documents

No documents have been uploaded by study researchers.