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Trial details imported from ClinicalTrials.gov

For full trial details, please see the original record at https://clinicaltrials.gov/study/NCT07039084




Registration number
NCT07039084
Ethics application status
Date submitted
18/06/2025
Date registered
26/06/2025
Date last updated
26/06/2025

Titles & IDs
Public title
Using a Speech-Generating Device to Support Communication in Childhood Dementia
Scientific title
A Randomized Cross-over Trial Examining the Efficacy of Implementing a Speech-generating Device for Childhood Dementia
Secondary ID [1] 0 0
115839
Universal Trial Number (UTN)
Trial acronym
Linked study record

Health condition
Health condition(s) or problem(s) studied:
Childhood Dementia 0 0
Genetic Disease 0 0
Nonverbal Communication 0 0
Augmentative and Alternative Communication 0 0
Condition category
Condition code
Neurological 0 0 0 0
Dementias
Neurological 0 0 0 0
Alzheimer's disease
Human Genetics and Inherited Disorders 0 0 0 0
Other human genetics and inherited disorders

Intervention/exposure
Study type
Interventional
Description of intervention(s) / exposure
Treatment: Devices - Speech-generating device
Other interventions - Control

Other: Treatment then Control - The arm receives the intervention (device), then the control

Other: Control then Treatment - The arm receives the control, then the treatment (device)


Treatment: Devices: Speech-generating device
The device is an iPad loaded with a grid-based and speech-generating communication application - a suitable application for the participant is determined at the beginning of the trial. This device is used in all 12 therapy sessions and implemented by a qualified speech pathologist in a natural, play-based setting.

Other interventions: Control
Participants will continue their current model of care. This means that if participants are receiving speech therapy locally, they may continue to do so given that no speech-generating device is introduced or used during this time. Participants will check in with the researching clinician at least once a week via telehealth or phone call - the aim is to stay in contact with families and reduce loss to follow-up. The clinician will also monitor treatment integrity and document any differences that may be present during this phase.

Intervention code [1] 0 0
Treatment: Devices
Intervention code [2] 0 0
Other interventions
Comparator / control treatment
Control group

Outcomes
Primary outcome [1] 0 0
Changes in the frequency of target communicative act related to the patient-defined outcome determined at the beginning of the trial
Timepoint [1] 0 0
Baseline, Week 0, Week 6 and Week 12
Secondary outcome [1] 0 0
Changes in overall communicative acts
Timepoint [1] 0 0
Baseline, Week 0, Week 6 and Week 12
Secondary outcome [2] 0 0
Changes in parent-reported communication via the Communication Matrix total score
Timepoint [2] 0 0
Baseline, Week 0, Week 6 and Week 12
Secondary outcome [3] 0 0
Changes in family and caregiver impact assessed via the Family Impact of Assistive Technology Scale for Augmentative and Alternative Communication (FIATS-AAC)
Timepoint [3] 0 0
Baseline, Week 0, Week 6 and Week 12
Secondary outcome [4] 0 0
Changes in family and caregiver impact assessed via semi-structured interviews
Timepoint [4] 0 0
Baseline, Week 6 and Week 12
Secondary outcome [5] 0 0
Changes in Language / Communication Competence assessed via the Low-Verbal Investigatory Survey
Timepoint [5] 0 0
Baseline, Week 0, Week 6 and Week 12

Eligibility
Key inclusion criteria
* Is between the ages of 3 and 12 years, inclusive, at the time of enrolment
* Has a genetically confirmed Childhood Dementia (via genetic report from a qualified geneticist), meeting the definition outlined in Elvidge et al. (2023) or is a condition listed on https://www.childhooddementia.org/what-is-childhood-dementia/childhood-dementia-disorders
* Passes a visual-motor screening test, therefore being able to tap on an iPad spontaneously or by imitation and has adequate hearing
* Considered "minimally verbal" with less than 20 spontaneous words (or gestalts) at baseline assessments, confirmed with the LVIS.
* Is not currently using a speech-generating device with proficiency (i.e. using the device as a main mode of communication on a daily basis).
* Is English-speaking or consents to therapy being conducted in English (parents will need to be able to complete the parent-reported measures in English)
Minimum age
3 Years
Maximum age
12 Years
Sex
Both males and females
Can healthy volunteers participate?
No
Key exclusion criteria
* Has an additional or dual genetic variation (as this is likely to cause multiple complications and increase variability),
* Is extremely ill or has progressed into a later stage of their disease (i.e. child has clinically significant loss of vision, hearing, fine motor skills, or is unable to adequately attend sessions due to illness),
* This is to ensure treatment is beneficial, reduce harm and reduce attrition rates.
* Lives outside of the state of Victoria (making it difficult for in-person appointments)
* Inability or unwillingness of participant or legally acceptable representative to give written informed consent.

Study design
Purpose of the study
Other
Allocation to intervention
Randomised controlled trial
Procedure for enrolling a subject and allocating the treatment (allocation concealment procedures)
Methods used to generate the sequence in which subjects will be randomised (sequence generation)
Masking / blinding
Blinded (masking used)
Who is / are masked / blinded?


The people assessing the outcomes
Intervention assignment
Crossover
Other design features
Phase
Not applicable
Type of endpoint/s
Statistical methods / analysis

Recruitment
Recruitment status
Not yet recruiting
Data analysis
Reason for early stopping/withdrawal
Other reasons
Date of first participant enrolment
Anticipated
Actual
Date of last participant enrolment
Anticipated
Actual
Date of last data collection
Anticipated
Actual
Sample size
Target
Accrual to date
Final
Recruitment in Australia
Recruitment state(s)
VIC
Recruitment hospital [1] 0 0
Murdoch Children's Research Institute - Melbourne
Recruitment postcode(s) [1] 0 0
- Melbourne

Funding & Sponsors
Primary sponsor type
Other
Name
Murdoch Childrens Research Institute
Address
Country

Ethics approval
Ethics application status

Summary
Brief summary
Trial website
Trial related presentations / publications
Public notes

Contacts
Principal investigator
Name 0 0
Address 0 0
Country 0 0
Phone 0 0
Fax 0 0
Email 0 0
Contact person for public queries
Name 0 0
Angela T Morgan
Address 0 0
Country 0 0
Phone 0 0
+61 (03) 8341 6458
Fax 0 0
Email 0 0
Contact person for scientific queries

Data sharing statement
Will individual participant data (IPD) for this trial be available (including data dictionaries)?
Yes
What data in particular will be shared?
The de-identified data set collected for the analysis of this trial will be made available 12 months following analysis and publication of the primary outcome. The following will be made available long-term for use by future researchers from a recognised research institution:

* Individual participant data that underlie the results reported after anonymisation/deidentification (text, tables, figures and appendices),
* Trial protocol, Participant Information and Consent Form (PICF),
* Statistical Analysis Plan (SAP), statistical code. Note that the data sharing of de-identified speech and language data is an Optional Consent for participants.

Supporting document/s available: Study protocol, Statistical analysis plan (SAP), Informed consent form (ICF), Analytic code
When will data be available (start and end dates)?
12 months after publication of primary outcome
Available to whom?
Interested researchers may request access to the data by submitting a formal data sharing request to the Sponsor. The request will be reviewed by the Sponsor and the Sponsor-Investigator, and any relevant Murdoch Children's Research Institute (MCRI) data sharing committee, considering factors such as scientific merit, data security, and adherence to the approved research objectives. The data may be obtained from MCRI by emailing [email protected]
Available for what types of analyses?
How or where can data be obtained?


What supporting documents are/will be available?

No Supporting Document Provided


Results publications and other study-related documents

No documents have been uploaded by study researchers.